B/BE/24/BVW5 - Informatie fiche bestemd voor het publiek (voorbereid door de kennisgever)

File: 
PDF icon bbe24bvw5_pub_nl.pdf
Trial reference: 
Phase 3, open-label, single-arm study to evaluate efficacy and safety of FIX gene transfer with PF-06838435 (rAAV-Spark100-hFIX-R338L) in adult male participants with moderately severe to severe hemophilia B (FIX:C ≤2%) (BeneGene-2)
Doc type: 
Information for the public