Gene therapy: main approaches and biosafety issues

At the end of the course, participants should be able to:

• get an accurate understanding of:
• gene therapy
• gene therapy main approaches
• gene vector
• perform a risk assessment of gene therapy conditions (this capacity will be tested through a group work on study cases)

The training will focus on:

• the main approaches in gene therapy (using various gene vectors), with an attention paid on the biosafety aspects in research and development laboratories, as well as on the risk for the patient
• the viral vectors used frequently in current gene therapy project, with the aim to point out their respective benefits in term of efficacy and safety